We use cookies to provide you with a better experience. By continuing to browse the site you are agreeing to our use of cookies in accordance with our Cookie Policy.
Accept
Home » FDA Spells Out Challenges for Sponsors of Therapies for Certain Rare Diseases
FDA Spells Out Challenges for Sponsors of Therapies for Certain Rare Diseases
The FDA detailed how sponsors can support the effectiveness of investigational new drugs or new drug uses for treatment of certain rare diseases, in final guidance published Friday.