Home » Biogen’s Gene Therapy Treating Retinal Disease Falters in Late-Stage Trial
Biogen’s Gene Therapy Treating Retinal Disease Falters in Late-Stage Trial
Biogen said its investigational gene therapy for a rare retinal disease failed to meet expectations in a phase 3 clinical trial.
The company is studying timrepigene emparvovec as a potential treatment of choroideremia, an inherited retinal disorder that causes progressive vision loss and ultimately blindness.
But the trial fell short of the primary endpoint of at least a 15-letter improvement in corrected vision after 12 months and failed to demonstrate efficacy for secondary endpoints.
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